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Welander (Late onset type I) Distal Myopathy

DigenicAutosomal DominantMuscular DystrophyOMIM 603518
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Overview

From WUSTL Neuromuscular

● Epidemiology Especially common: Mid-Sweden & Finland gene frequency 1/4000 Penetrance: Relatively low due to late age of onset Genetics 10 Mutation: Glu384Lys Finnish & Swedish patients have shared haplotype Homozygotes: Weakness is more severe & proximal Allelic disorders ALS-FTD (ALS 26) Digenic Distal myopathy 53 TIA1 mutation: Asn357Ser SQSTM1 mutation: Pro392Leu most common MYH7 related myopathies: Asn357Ser TIA1 protein (Nucleolysin TIA-1 isoform p40) Nucleic acid-binding protein: Preferentially recognizes poly(A) homopolymers Induces DNA fragmentation in permeabilized thymocytes Compo

OMIM Entries

OMIM #603518OMIM #619133

Related Conditions

Shared genes
ALS Genes: Hereditary & Susceptibility
FTDPD2PD1

External Resources

WUSTL Neuromuscular
Washington University Disease Center
OMIM
Online Mendelian Inheritance in Man
PubMed
Biomedical Literature
GeneReviews
NCBI Expert-Authored Reviews
Orphanet
Portal for Rare Diseases
NORD
National Organization for Rare Disorders

Data sourced from the Washington University Neuromuscular Disease Center. For clinical use, always refer to primary sources.