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Vocal Cord & Pharyngeal Weakness (MPD2; VCPDM; ALS21; MSP5)

Autosomal DominantMuscular DystrophyOMIM 164015
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Overview

From WUSTL Neuromuscular

● Nosology Multisystem proteinopathy 5 (MSP5) Reclassified as ALS21 Epidemiology: 16 families Genetics 22 Mutation: Ser85Cys Allelic disorders Familial ALS 21, Dominant Fronto-Temporal Dementia Mutation: Retrotransposed Full-Length Transcript of Matrin-3 Variant 5 Matrin 3 protein 46 Cell location Nuclear matrix Inner face of nuclear envelope May move to cytoplasm in diseased cells Tissue expression: Muscle & Other tissues Contains RNA-DNA binding motif Interacts with Proteins: TDP-43; DHX9 ; PABN1 DNA sequences: Repetitive; Adenine/Thymine-rich RNA: RNA stabilized by MATR3 binding Self associ

OMIM Entries

OMIM #164015OMIM #603115OMIM #606070

Related Conditions

Shared genes
FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY 1A (FSHMD 1A)
DNMT3BLRIF1SMALL
HERPES ZOSTER (Varicella)
VZVDNAC6
Nuclei: Muscle Fibers
DNA
Oculopharyngodistal Myopathies (OPDM)
AS1DISEASEDNA

External Resources

WUSTL Neuromuscular
Washington University Disease Center
OMIM
Online Mendelian Inheritance in Man
PubMed
Biomedical Literature
GeneReviews
NCBI Expert-Authored Reviews
Orphanet
Portal for Rare Diseases
NORD
National Organization for Rare Disorders

Data sourced from the Washington University Neuromuscular Disease Center. For clinical use, always refer to primary sources.