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SMA 5q: Classification (without treatment)

Autosomal RecessiveDe NovoMitochondrialX-LinkedVariableMotor Neuron / ALSOMIM 164017
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Overview

From WUSTL Neuromuscular

Inheritance: Recessive SMN1 mutations: Bi-Allelic SMAType SMN2Copies SMA5q % OnsetAge MotorMilestoneAchieved LifeExpectancy 0 1 < 1% Birth Never Sit < 6 mo 1 2-3 55% 0 to 6 mo Never Sit 8 to 24 mo 2 2-4 30% 6 to 18 mo Sit 2 to 4 decades 3 3-5 10% 3A: 1.5 to 3 yrs 3B: 3 to 20 yrs Walk Normal 4 3-5 5% Adult Walk Normal History SMA described independently by Guido Werdnig & Hoffmann in 1891 Werdnig Described condition as "Neurogenic dystrophy" Hoffmann Established spinal nature of SMA Coined term: "Spinale muskelatrophie" Epidemiology Incidence of SMA disease: 1 in 6,000 to 20,000 births 25 2nd m

OMIM Entries

OMIM #164017OMIM #600812OMIM #300131OMIM #606722OMIM #600355OMIM #601748OMIM #603011OMIM #602595OMIM #606168OMIM #134795OMIM #176590OMIM #601627OMIM #600354OMIM #253300OMIM #253550OMIM #253400OMIM #271150

Related Conditions

Shared genes
C. Anti-GM1 Antibodies
GM1IGMGM1LMN
Treatment with
GM1LMN

External Resources

WUSTL Neuromuscular
Washington University Disease Center
OMIM
Online Mendelian Inheritance in Man
PubMed
Biomedical Literature
GeneReviews
NCBI Expert-Authored Reviews
Orphanet
Portal for Rare Diseases
NORD
National Organization for Rare Disorders

Data sourced from the Washington University Neuromuscular Disease Center. For clinical use, always refer to primary sources.