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Neuroaxonal Dystrophy (Late infantile; NBIA2A)

Autosomal RecessiveMitochondrialNeuropathy (Hereditary)OMIM 256600
W
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Overview

From WUSTL Neuromuscular

● Nosology: Seitelberger�s disease; Neurodegeneration with brain iron accumulation 2A Epidemiology: Multiple families Genetics PLA2G6 mutations: V691del; Tyr790Ter; Lys545Thr; Val310Glu; Arg632Trp (Karak syndrome) Allelic disorders Atypical Neuroaxonal Dystrophy: Childhood onset Karak syndrome (NBIA2B) Neurodegeneration with brain iron accumulation 2 (NBIA2A) Parkinson Disease 14, Recessive (PARK14; Dystonia-Parkinson, Adult) Spastic-Ataxia PLA2 enzymes General: Catalyze release of fatty acids from phospholipids PLA2G6 activity high in brain PLA2G6 mutations: Most probably cause loss of functi

Associated Genes

PANK2
pantothenate kinase 2
20p13

OMIM Entries

OMIM #256600OMIM #603604OMIM #610217OMIM #612953OMIM #234200OMIM #606157OMIM #609241OMIM #609242OMIM #104170OMIM #606159OMIM #134790

External Resources

WUSTL Neuromuscular
Washington University Disease Center
OMIM
Online Mendelian Inheritance in Man
PubMed
Biomedical Literature
GeneReviews
NCBI Expert-Authored Reviews
Orphanet
Portal for Rare Diseases
NORD
National Organization for Rare Disorders

Data sourced from the Washington University Neuromuscular Disease Center. For clinical use, always refer to primary sources.